Neuren Pharmaceuticals (ASX: NEU) specializes in developing novel treatments for severe neurodevelopmental disorders that manifest in early childhood, focusing on conditions with unmet medical needs due to impaired brain cell connections and signalling. The company has garnered significant expertise through years of clinical development. In partnership with Acadia Pharmaceuticals (NASDAQ: ACAD), Neuren has advanced DAYBUE™ (trofinetide), the first FDA-approved treatment for Rett syndrome in individuals aged two years and older. Additionally, Neuren is progressing its second drug candidate, NNZ-2591, through Phase 2 trials for Phelan-McDermid syndrome, Angelman syndrome, Pitt Hopkins syndrome, and Prader-Willi syndrome.
Neuren Pharmaceuticals (NEU:ASX)
Last update - 7 November 2024
By James Woods